UAE’s Medcare treats first international SMA patient with revolutionary intrathecal gene therapy
The newly licensed intrathecal gene therapy expands life-changing treatment options for children and adults affected by SMA
Medcare Women & Children Hospital has successfully administered a pioneering intrathecal gene therapy for Spinal Muscular Atrophy (SMA) to Hulus, a three-year-old patient from Turkey. This milestone positions Medcare among the first private healthcare providers worldwide to offer this innovative treatment to an older international patient, overcoming previous age and weight limitations.
SMA is a rare neuromuscular disorder that progressively weakens muscles responsible for movement and breathing. This newly licensedone-time therapy addresses the root genetic cause by delivering a functional SMN1 gene.
For Hulus...